Drug Guide

Generic Name

Tafamidis Meglumine

Brand Names Vyndaqel

Classification

Therapeutic: Treatment of transthyretin amyloid cardiomyopathy, transthyretin amyloidosis

Pharmacological: Tafamidis is a selective transthyretin stabilizer

FDA Approved Indications

  • Transthyretin amyloid cardiomyopathy (ATTR-CM)

Mechanism of Action

Tafamidis binds to the thyroxine-binding sites of transthyretin, stabilizing the tetramer and preventing dissociation into monomers that form amyloid deposits, thereby reducing amyloid formation and deposition.

Dosage and Administration

Adult: 80 mg once daily, with food

Pediatric: Not approved for pediatric use

Geriatric: No specific dose adjustment required, but caution in elderly patients

Renal Impairment: No dose adjustment needed for mild to moderate impairment; limited data in severe impairment

Hepatic Impairment: No dose adjustment specified

Pharmacokinetics

Absorption: Rapidly absorbed with peak plasma levels in approximately 1 hour

Distribution: Extensively bound to plasma proteins (~99%)

Metabolism: Primarily metabolized via glucuronidation; limited CYP involvement

Excretion: Excreted mainly in feces; minimal unchanged drug in urine

Half Life: Approximately 49 hours

Contraindications

  • Hypersensitivity to tafamidis or any component of the formulation

Precautions

  • Use with caution in hepatic impairment; monitor for adverse effects; pregnancy category C, risk cannot be ruled out; breast-feeding: no data available, consider risks

Adverse Reactions - Common

  • Increased liver enzymes (ALT, AST) (Less common)
  • Hypersensitivity reactions (Uncommon)

Adverse Reactions - Serious

  • Progressive multifocal leukoencephalopathy (very rare) (Rare)
  • Heart failure exacerbation (Rare)

Drug-Drug Interactions

  • No significant interactions reported

Drug-Food Interactions

  • No specific interactions

Drug-Herb Interactions

  • Limited data, caution advised

Nursing Implications

Assessment: Baseline liver function tests, cardiac function monitoring as appropriate

Diagnoses:

  • Risk for hepatic injury
  • Ineffective tissue perfusion related to amyloid cardiomyopathy

Implementation: Administer with food, monitor for side effects, educate patient about adherence and side effects

Evaluation: Assess symptom progression, monitor liver enzymes, evaluate for adverse reactions

Patient/Family Teaching

  • Take medication exactly as prescribed, with food
  • Report any signs of liver problems (jaundice, dark urine), allergic reactions, or unusual symptoms
  • Maintain regular follow-up appointments for monitoring

Special Considerations

Black Box Warnings:

  • No black box warnings currently

Genetic Factors: Genetic testing for transthyretin mutations may inform treatment

Lab Test Interference: Potential for elevated liver enzymes; monitor accordingly

Overdose Management

Signs/Symptoms: No specific overdose data, but watch for hypersensitivity or hepatic toxicity

Treatment: Supportive care; consider activated charcoal if ingestion recent; consult poison control

Storage and Handling

Storage: Store at room temperature between 20°C and 25°C (68°F to 77°F)

Stability: Stable at room temperature for up to 24 months

This guide is for educational purposes only and is not intended for clinical use.